Fortuity Pharma Information

Fortuity Pharma is a public-benefit corporation dedicated to developing effective and affordable therapies for the rare disease community by repurposing existing drugs and nutraceuticals. Inspired by the story of Lucia, a patient with WOREE syndrome, the company was founded to bring the discontinued drug amlexanox back to market after it showed significant therapeutic potential in treating her condition caused by nonsense mutations leading to a premature termination codon. There is significant preclinical evidence this drug can read through premature stops during DNA translation to mRNA and then to protein synthesis in many rare diseases, so Fortuity Pharma is eager to leverage the established safety profile of this drug to develop effective treatments for patients with this genotype.