Our mission is simple, yet powerful: To cure Multiple Sulfatase Deficiency. Multiple Sulfatase Deficiency (MSD) ia a rare genetic, progressive, neurodegenerative disease caused by the build up of cellular waste throughout the body leading to neurologic regression and multisystemic symptoms. Children with MSD rarely survive past their 13th birthday. Currently there is no treatment or cure available for MSD; however, there is hope. Various mutations of the SUMF1 gene are known to be the cause of MSD, and the knowledge of these specific gene mutations allows researchers and doctors to move forward and find a treatment and cure. Gene therapy could help slow the progression of the disease, and possibly deliver a cure. The United MSD Foundation is currently working with partner organizations, researchers, and doctors from all over the world to fund a first-in-human gene therapy clinical trial. Additional initiatives include continuing to identify patients worldwide, the development of a patient registry and biobank, and advocating for newborn screening across the United States.
| Website | http://www.curemsd.org |
| Employees | 19 (5 on RocketReach) |
| Founded | 2016 |
| Phone | +1 228-295-7084 |
| Industry | Non-profit Organizations, Charitable Organizations & Foundations, Organizations |
| Keywords | Rare Disease Research, Lysosomal Storage Disorders, Progressive Neurological Disease, Genetic Disease Treatment, Rare Disease Therapies, Clinical Trials, Genetic Disorders, Genetic Mutations, Enzyme Replacement Therapy, Drug Development, Medical Research, Pharmaceutical Research, Biotechnology, Disease Treatment, Medical Breakthroughs, Patient Advocacy |
| Competitors | Sanofi, Teva Pharmaceuticals, National MS Society, Acorda Therapeutics, Inc., MS Trust, Accelerated Cure Project for Multiple Sclerosis, MS International Federation (MSIF), Sierra Clinical Research, The Myelin Project, MS Research Australia +35 more (view full list) |
| SIC | SIC Code 839 Companies, SIC Code 83 Companies |
| NAICS | NAICS Code 813 Companies, NAICS Code 8132 Companies, NAICS Code 81321 Companies, NAICS Code 81 Companies |
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CureMSD Questions
Sarah Vandersypen is the Executive Director of CureMSD.
5 people are employed at CureMSD.
CureMSD is based in Biloxi, Mississippi.
The NAICS codes for CureMSD are [813, 8132, 81321, 81].
The SIC codes for CureMSD are [839, 83].
Top CureMSD Employees
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Sarah Vandersypen
Executive Director at CureMSD
Baton Rouge, LA, US22 -
11
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Kara Anseth
Volunteer Professional Ambassador at CureMSD
Colorado Springs, CO, US22
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