Cure MKD Information

Cure MKD is a patient-led foundation dedicated to transforming the landscape of Mevalonate Kinase Deficiency (MKD). Driven by a family’s reality of watching their daughter Gabriela battle numerous near-death encounters in the NICU, chronic hospitalizations, and severe disease flares, they refused to suffer in silence. They chose to act. Cure MKD was founded to aggressively bridge the gap between existing scientific potential and the life-saving treatments patients urgently need. Our mission is to relentlessly accelerate science and unify the global ecosystem to move from symptom management to a definitive cure for everyone living with Mevalonate Kinase Deficiency. Our Action Platform We are executing a rigorous, strategic roadmap to deliver a cure through three core pillars: Powering Research: We take a global approach and invest in teams that have a proven track record of taking the science out of the lab and delivering it to real patients. Unifying the Ecosystem: We act as the essential bridge, connecting patients, clinicians, researchers, regulators, and industry partners via standardized data, processes, and networks. Driving Strategic Action: We move processes in parallel rather than one after another, leading to faster results. The researchers are assembled. The roadmap is clear. Join our fight, explore our research pipeline, or fuel the cure by visiting our website below.